Session Learning Objectives:
1. Describe indications for gene therapy in sickle cell disease;
2. Understand the basic methods by which gene therapy affects hemoglobin;
3. Hear the patient’s perspective on the decision and process of undergoing gene therapy.

Presenters:
Amy Sobota, MD, MPH
Chief, Pediatric Hematology/Oncology
Boston Medical Center
Associate Professor of Pediatrics
Boston University Chobanian & Avedisian School of Medicine

and

Jovany Constand, Patient

Dr. Sobota and Mr. Constand have nothing to disclose and does not plan on discussing unlabeled/investigational uses of a commercial product.